If CRISPR stays active too long, it could cut unintended parts of the genome. To reduce this risk, the researchers designed a self-inactivating CRISPR system. This means that CRISPR edits the gene and ...
9 min read |New research in a HD mouse model points to a key culprit: a small fragment called HTT1a. Lowering HTT1a levels successfully delayed disease signs in mice that model HD, perhaps shaping the ...
Artificial Intelligence, or AI, has become an everyday feature of the world we live in. Internet browsers have an ‘AI mode’ and even our refrigerators and vacuum cleaners now include AI features!
A small study based in Ireland asked a simple question: what does caring for someone with Huntington’s disease feel like? The answers point to isolation, stigma, and major gaps in healthcare support ...
A new collaboration between researchers at Indiana University Southeast and Bellarmine University in Kentucky, both in the USA, aimed to investigate what happens when a physical therapist and a music ...
⏱️ 6 min read | Today, on Gratitude Day, we share a guest piece from HD researcher Roy Maimon that Huntington’s disease is neuroscience’s best investment, not just for its scientific clarity, but for ...
Every day, we reach for hundreds of things without thinking twice. For people with Huntington’s disease (HD), those everyday movements could carry hidden information about how the disease is ...
Some of the biggest news of the month came on March 2nd, when uniQure relayed communications from the U.S. Federal Drug Administration (FDA). The FDA does not believe that uniQure’s current Phase 1/2 ...