Wugen Announces Dosing of First Patients in Pivotal Trial of Off-the-Shelf, Allogeneic, CD7-Targeted CAR-T Cell Therapy WU-CART-007
Previously reported Phase 1/2 data on WU-CART-007 demonstrated clinically manageable safety and evidence of anti-leukemic activity with an ...
Endpoints News4d
Re­genxbio shares new Duchenne gene ther­a­py da­ta ahead of big read­out next year
Regenxbio reports promising microdystrophin expression data in DMD patients, with highest levels in 3-year-old. Plans FDA ...
Endpoints News5d
Six­teen-year-old dies af­ter re­ceiv­ing Sarep­ta’s Duchenne gene ther­a­py
A teenage boy who received Sarepta’s Duchenne muscular dystrophy gene therapy Elevidys died from liver failure, the biotech ...
BioPharma Dive5d
Arbor raises $74M amid genetic medicine’s funding slump
The round will fund a “one-and-done” treatment for a rare kidney condition that its CEO says can address concerns patients ...