A new nonprofit wants to streamline gene therapy for diseases often avoided by pharmaceutical companies — making treatment ...
A coalition of biotech firms is lobbying to exclude orphan drugs from new federal pilot programs aimed at lowering Medicare ...
The Broad Institute, Boston Children’s Hospital, and Maine’s Jackson Laboratory announced a collaboration to develop rare ...
Chan Zuckerberg Initiative's Biohub will offer new grants to the rare disease community while expanding its AI drug repurposing partnership with Every Cure.
Rare-disease families can now invest in Mahzi Therapeutics' gene therapy, giving patients a financial stake in developing ...
Anthropic is betting that AI can make a difference in rare disease research. It has launched a new programme through which it ...
Plasma exchange can help treat people with a rare inflammatory disease that can cause blindness, according to a systematic ...
Primary biliary cholangitis is a rare autoimmune disease that affects the liver and can progress to cirrhosis. It occurs when ...
The seven-year medical odyssey that once defined rare disease diagnosis is being rewritten by algorithms capable of identifying medical zebras in the time it takes to refresh your social media feed.
An adult in Lincoln County has tested positive for the virus, marking Maine's third confirmed case this year.
Scientists from the University of Edinburgh carried out the first major genetic study of the community.
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